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基因点突变细胞,对于疾病的预测、研究与治疗都能够发挥作用。例如点突变细胞株可用于神经疾病变性机制研究,小分子药物研发,肿瘤诊断与治疗,遗传性疾病诊断登。除此之外,还有基因点突变载体构建的相关服务,感兴趣的话请前往进行查询。
Generation of Human Isogenic Induced Pluripotent Stem Cell Lines with CRISPR Prime Editing
Structural basis for pegRNA-guided reverse transcription by a prime editor
A truncated reverse transcriptase enhances prime editing by split AAV vectors
Structural basis for pegRNA-guided reverse transcription by a prime editor
Ex vivo prime editing of patient haematopoietic stem cells rescues sickle-cell disease phenotypes after engraftment in mice